Patient-reported outcomes on familial amyloid polyneuropathy (FAP)

Transthyretin familial amyloid polyneuropathy (ATTR-FAP) is a rare autosomal dominant inherited disease affecting multiple organ systems. ATTR-FAP patients ’ experiences have rarely been documented. The aim of ...

Source: Orphanet Journal of Rare Diseases - October 14, 2020 Category: Internal Medicine Authors: Fabian J. Bolte, Christel Langenstroer, Frauke Friebel, Anna H üsing-Kabar, Martin Dugas and Hartmut H. Schmidt Tags: Research Source Type: research