Observational Study to Assess Endpoint Operational Feasibility & Measurement Properties in Retinitis Pigmentosa Patients
Conditions: Retinitis Pigmentosa Sponsors: Ray Therapeutics, Inc.; The Vision Research and Assessment Institute (VRAI) Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 19, 2024 Category: Research Source Type: clinical trials

Clinical and Genetic Findings in Patients With PRPF31-associated Retinitis Pigmentosa
Conditions: Retinitis Pigmentosa Sponsors: University Hospital Tuebingen Completed (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 16, 2024 Category: Research Source Type: clinical trials

A Study Comparing Two Doses of AGTC-501 in Male Subjects With X-linked Retinitis Pigmentosa Caused by RPGR Mutations (SKYLINE)
Conditions: X-Linked Retinitis Pigmentosa Interventions: Biological: rAAV2tYF-GRK1-RPGR Sponsors: Beacon Therapeutics Active, not recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 27, 2024 Category: Research Source Type: clinical trials

Natural History Study in Patients With PDE6A-, PDE6B- and RHO-linked Retinitis Pigmentosa
Conditions: Retinitis Pigmentosa Sponsors: University Hospital Tuebingen Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 21, 2024 Category: Research Source Type: clinical trials

The Effects of Disulfiram (Antabuse ®) on Visual Acuity in Patients With Retinal Degeneration
Conditions: Alcohol Use Disorder; Retinal Dystrophies; Age-Related Macular Degeneration; Retinitis Pigmentosa; Stargardt Disease Interventions: Drug: Oral disulfiram Sponsors: University of Rochester Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 20, 2024 Category: Research Source Type: clinical trials

Biomarkers in Retinitis Pigmentosa
Conditions: Retinitis Pigmentosa Interventions: Diagnostic Test: OCT, OCT angiography, flicker ERG and Ultra Wide Field retinography and autofluorescence. Sponsors: Fondazione Policlinico Universitario Agostino Gemelli IRCCS Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 12, 2024 Category: Research Source Type: clinical trials

Safety and Efficacy Study of Novel Gene Therapy ZM-02 for Retinitis Pigmentosa Patients
Conditions: Retinitis Pigmentosa Interventions: Drug: ZM-02-L; Drug: ZM-02-H; Procedure: ZM-02-S Sponsors: Zhongmou Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 5, 2024 Category: Research Source Type: clinical trials

Safety and Tolerability of Intravitreal Administration of VG901 in Patients With Retinitis Pigmentosa Due to Mutations in the CNGA1 Gene
Conditions: Retinitis Pigmentosa Interventions: Drug: VG901 Sponsors: ViGeneron GmbH Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 4, 2024 Category: Research Source Type: clinical trials

DAWN: A Phase 2 Multi-center Study Comparing Two Doses of AGTC-501 in Male Participants With X-linked Retinitis Pigmentosa Who Have Been Previously Treated With an AAV Vector-based Gene Therapy Designed to Provide Full-length Functioning RPGR Protein
Conditions: X-Linked Retinitis Pigmentosa Interventions: Biological: AGTC-501 (high dose and standard corticosteroid regimen); Biological: AGTC-501 (low dose and standard corticosteroid regimen); Biological: AGTC-501 (high dose and modified corticosteroid regimen) Sponsors: Beacon Therapeutics Enrolling by invitation (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 23, 2024 Category: Research Source Type: clinical trials

Beacon Therapeutics Announces Positive 12-Month Data from Phase 2 SKYLINE Trial of AGTC-501 in Patients with X-Linked Retinitis Pigmentosa
London, UK, Cambridge, MA, 08 February 2024– Beacon Therapeutics Holdings Limited (‘Beacon Therapeutics’ or‘the Company’), a leading ophthalmic gene therapy company with a mission to save and restore the vision of... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - February 8, 2024 Category: Pharmaceuticals Source Type: clinical trials

Safety and Efficacy of Stem Cell Small Extracellular Vesicles in Patients With Retinitis Pigmentosa
Conditions: Retinitis Pigmentosa Interventions: Biological: GMP compliant-BM-MSC derived sEVs Sponsors: Mahidol University Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 5, 2024 Category: Research Source Type: clinical trials

Transpalpebral electrical stimulation for the treatment of retinitis pigmentosa: study protocol for a series of N-of-1 single-blind, randomized controlled trial
DiscussionThe trial will evaluate the efficacy and safety of microcurrent stimulation on RP and provide high-quality evidence for clinical application through N-of-1 trial.Trial registrationChinese Clinical Trial Registry; ChiCTR2300067357;https://www.chictr.org.cn/showproj.html?proj=174635.  Registered on 5 January 2023 (Source: Trials)
Source: Trials - January 27, 2024 Category: Research Source Type: clinical trials

Coloured-light in Retinitis Pigmentosa.
Conditions: Retinitis Pigmentosa Interventions: Device: Coloured-light torch; Device: Different coloured-light torch Sponsors: University College, London Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 25, 2024 Category: Research Source Type: clinical trials

Non-Interventional Long Term Follow-up Study of Participants Previously Enrolled in the RESTORE Study
Conditions: Retinitis Pigmentosa; Retinitis; Retinal Diseases; Eye Diseases; Eye Diseases, Hereditary; Retinal Dystrophies; Retinal Degeneration Interventions: Biological: Gene Therapy product-MCO-010 Sponsors: Nanoscope Therapeutics Inc. Enrolling by invitation (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 8, 2023 Category: Research Source Type: clinical trials

Evaluation of New Head-mounted Visual Aids Among Patients With Low Vision
Conditions: Glaucoma; Age-related Macular Degeneration; Retinitis Pigmentosa; Diabetic Retinopathy Interventions: Device: New head-mounted visual aids Sponsors: Zhongshan Ophthalmic Center, Sun Yat-sen University Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 11, 2023 Category: Research Source Type: clinical trials