Retraction Note: Long noncoding RNA RBMS3-AS3 acts as a microRNA-4534 sponge to inhibit the progression of prostate cancer by upregulating VASH1
Gene Therapy, Published online: 09 January 2024; doi:10.1038/s41434-023-00439-5Retraction Note: Long noncoding RNA RBMS3-AS3 acts as a microRNA-4534 sponge to inhibit the progression of prostate cancer by upregulating VASH1 (Source: Gene Therapy)
Source: Gene Therapy - January 9, 2024 Category: Genetics & Stem Cells Authors: Zhenming Jiang Yuxi Zhang Xi Chen Pingeng Wu Dong Chen Source Type: research
CRISPR/Cas9-mediated base editors and their prospects for mitochondrial genome engineering
Gene Therapy, Published online: 04 January 2024; doi:10.1038/s41434-023-00434-wCRISPR/Cas9-mediated base editors and their prospects for mitochondrial genome engineering (Source: Gene Therapy)
Source: Gene Therapy - January 4, 2024 Category: Genetics & Stem Cells Authors: Shahin Eghbalsaied Clancy Lawler Bj örn Petersen Raul A. Hajiyev Steve R. Bischoff Stephen Frankenberg Source Type: research
Ghrelin mediated cardioprotection using in vitro models of oxidative stress
Gene Therapy, Published online: 04 January 2024; doi:10.1038/s41434-023-00435-9Ghrelin mediated cardioprotection using in vitro models of oxidative stress (Source: Gene Therapy)
Source: Gene Therapy - January 4, 2024 Category: Genetics & Stem Cells Authors: Cindy Y. Kok George Ghossein Sindhu Igoor Renuka Rao Tracy Titus Shinya Tsurusaki James JH. Chong Eddy Kizana Source Type: research
Correction: Cost of gene therapy
Gene Therapy, Published online: 04 January 2024; doi:10.1038/s41434-023-00432-yCorrection: Cost of gene therapy (Source: Gene Therapy)
Source: Gene Therapy - January 4, 2024 Category: Genetics & Stem Cells Authors: Patrick T. Harrison Theodore Friedmann Source Type: research
CSTB gene replacement improves neuroinflammation, neurodegeneration and ataxia in murine type 1 progressive myoclonus epilepsy
Gene Therapy, Published online: 22 December 2023; doi:10.1038/s41434-023-00433-xCSTB gene replacement improves neuroinflammation, neurodegeneration and ataxia in murine type 1 progressive myoclonus epilepsy (Source: Gene Therapy)
Source: Gene Therapy - December 22, 2023 Category: Genetics & Stem Cells Authors: Emrah Gumusgoz Sahba Kasiri Mayank Verma Jun Wu Daniel Villarreal Acha Ummay Marriam Sharyl Fyffe-Maricich Amy Lin Xin Chen Steven J. Gray Berge A. Minassian Source Type: research
Distributional comparison of different AAV vectors after unilateral cochlear administration
Gene Therapy, Published online: 14 December 2023; doi:10.1038/s41434-023-00431-zDistributional comparison of different AAV vectors after unilateral cochlear administration (Source: Gene Therapy)
Source: Gene Therapy - December 14, 2023 Category: Genetics & Stem Cells Authors: Shuang Han Zhijiao Xu Shengyi Wang Honghai Tang Shaowei Hu Hui Wang Guofang Guan Yilai Shu Source Type: research
Looking ahead: ethical and social challenges of somatic gene therapy for sickle cell disease in Africa
Gene Therapy, Published online: 27 November 2023; doi:10.1038/s41434-023-00429-7Looking ahead: ethical and social challenges of somatic gene therapy for sickle cell disease in Africa (Source: Gene Therapy)
Source: Gene Therapy - November 27, 2023 Category: Genetics & Stem Cells Authors: Nchangwi Syntia Munung Obiageli E. Nnodu Patrick Ohiani Moru Akpaka A. Kalu Benido Impouma Marsha J. Treadwell Ambroise Wonkam Source Type: research
Engineered compact pan-neuronal promoter from Alphaherpesvirus LAP2 enhances target gene expression in the mouse brain and reduces tropism in the liver
Gene Therapy, Published online: 27 November 2023; doi:10.1038/s41434-023-00430-0Engineered compact pan-neuronal promoter from Alphaherpesvirus LAP2 enhances target gene expression in the mouse brain and reduces tropism in the liver (Source: Gene Therapy)
Source: Gene Therapy - November 27, 2023 Category: Genetics & Stem Cells Authors: Carola J. Maturana Source Type: research
Modeling Glutaric Aciduria Type I in human neuroblastoma cells recapitulates neuronal damage that can be rescued by gene replacement
Gene Therapy, Published online: 20 November 2023; doi:10.1038/s41434-023-00428-8Modeling Glutaric Aciduria Type I in human neuroblastoma cells recapitulates neuronal damage that can be rescued by gene replacement (Source: Gene Therapy)
Source: Gene Therapy - November 20, 2023 Category: Genetics & Stem Cells Authors: A. Mateu-Bosch E. Segur-Bailach J. Garc ía-Villoria S. Gea-Sorl í I. Ruiz J. del Rey J. Camps M. Guitart-Mampel G. Garrabou F. Tort A. Ribes C. Fillat Source Type: research
Overexpression of KCNN4 channels in principal neurons produces an anti-seizure effect without reducing their coding ability
Gene Therapy, Published online: 15 November 2023; doi:10.1038/s41434-023-00427-9Overexpression of KCNN4 channels in principal neurons produces an anti-seizure effect without reducing their coding ability (Source: Gene Therapy)
Source: Gene Therapy - November 15, 2023 Category: Genetics & Stem Cells Authors: Evgeny S. Nikitin Tatiana Y. Postnikova Elena Y. Proskurina Anastasia A. Borodinova Violetta Ivanova Matvey V. Roshchin Maria P. Smirnova Ilya Kelmanson Vsevolod V. Belousov Pavel M. Balaban Aleksey V. Zaitsev Source Type: research
Cost of gene therapy
Gene Therapy, Published online: 08 November 2023; doi:10.1038/s41434-023-00408-yCost of gene therapy (Source: Gene Therapy)
Source: Gene Therapy - November 8, 2023 Category: Genetics & Stem Cells Authors: Patrick Harrison Theodore Friedmann Source Type: research
The estimated annual financial impact of gene therapy in the United States
Gene Therapy, Published online: 08 November 2023; doi:10.1038/s41434-023-00419-9The estimated annual financial impact of gene therapy in the United States (Source: Gene Therapy)
Source: Gene Therapy - November 8, 2023 Category: Genetics & Stem Cells Authors: Chi Heem Wong Dexin Li Nina Wang Jonathan Gruber Andrew W. Lo Rena M. Conti Source Type: research
Successes and challenges in clinical gene therapy
Gene Therapy, Published online: 08 November 2023; doi:10.1038/s41434-023-00390-5Successes and challenges in clinical gene therapy (Source: Gene Therapy)
Source: Gene Therapy - November 8, 2023 Category: Genetics & Stem Cells Authors: Donald B. Kohn Yvonne Y. Chen Melissa J. Spencer Source Type: research
Towards affordable CRISPR genomic therapies: a task force convened by the Innovative Genomics Institute
Gene Therapy, Published online: 08 November 2023; doi:10.1038/s41434-023-00392-3Towards affordable CRISPR genomic therapies: a task force convened by the Innovative Genomics Institute (Source: Gene Therapy)
Source: Gene Therapy - November 8, 2023 Category: Genetics & Stem Cells Authors: Lea Witkowsky Matthew Norstad Audrey R. Glynn Melinda Kliegman Source Type: research
Access to affordable medicines: obligations of universities and academic medical centers
Gene Therapy, Published online: 08 November 2023; doi:10.1038/s41434-023-00393-2Access to affordable medicines: obligations of universities and academic medical centers (Source: Gene Therapy)
Source: Gene Therapy - November 8, 2023 Category: Genetics & Stem Cells Authors: Steven Joffe Rena M. Conti Jorge L. Contreras Emily A. Largent Holly Fernandez Lynch David Mitchell Rachel E. Sachs Allison M. Whelan Matthew S. McCoy Source Type: research
