Gene Therapy: A ' One and Done ' Hemophilia B Treatment? Gene Therapy: A ' One and Done ' Hemophilia B Treatment?

Nearly all patients treated with a one-time gene therapy shot for hemophilia B were able to discontinue full-dose bleeding prophylaxis, says a study. Annual bleed rates fell by 64% after the lead-in period.Medscape Medical News
Source: Medscape Hematology-Oncology Headlines - Category: Cancer & Oncology Tags: Hematology-Oncology News Source Type: news