FDA Approves First Drug for Rare Inherited Anemia FDA Approves First Drug for Rare Inherited Anemia

Mitapivat (Pyrukynd) is the first disease-modifying agent for hemolytic anemia in adults with pyruvate kinase (PK) deficiency.FDA Approvals
Source: Medscape Hematology-Oncology Headlines - Category: Cancer & Oncology Tags: Hematology-Oncology News Alert Source Type: news