P011. Impact of Patisiran on Activities of Daily Living and Functional Status in hATTR Amyloidosis
Hereditary transthyretin-mediated (hATTR) amyloidosis, a rare, multi-systemic, life-threatening disease, causes neurologic and cardiac dysfunction, leading to impaired functional status and declining ability to perform activities of daily living (ADLs).
Source: Heart and Lung - Category: Intensive Care Authors: Madeline Merkel, David Adams, Senda Ajroud-Driss, John Berk, Alejandra Gonzalez-Duarte, Cecilia Hale, Hollis Lin, Amanda Peltier, Ole Suhr, Ivailo Tournev, Taro Yamashita Tags: Research Source Type: research