P011. Impact of Patisiran on Activities of Daily Living and Functional Status in hATTR Amyloidosis

Hereditary transthyretin-mediated (hATTR) amyloidosis, a rare, multi-systemic, life-threatening disease, causes neurologic and cardiac dysfunction, leading to impaired functional status and declining ability to perform activities of daily living (ADLs).
Source: Heart and Lung - Category: Intensive Care Authors: Tags: Research Source Type: research