Optimizing language for effective communication of gene therapy concepts with hemophilia patients: a qualitative study

For communities of people living with hemophilia and other genetic conditions, gene therapy could represent a paradigm shift in treatment strategies. As investigational therapeutic modalities such as gene ther...

Source: Orphanet Journal of Rare Diseases - April 28, 2021 Category: Internal Medicine Authors: Daniel P. Hart, Brian R. Branchford, Sarah Hendry, Robert Ledniczky, Robert F. Sidonio Jr., Claude N égrier, Michelle Kim, Michelle Rice, Matthew Minshall, Claire Arcé, Steve Prince, Maria Kelleher and Sharon Lee Tags: Research Source Type: research