“I have SMA, SMA doesn’t have me”: a qualitative snapshot into the challenges, successes, and quality of life of adolescents and young adults with SMA

With the approval of three treatments for spinal muscular atrophy (SMA) and several promising therapies on the horizon, the SMA adolescent and young adult populations are expected to evolve in the coming years...

Source: Orphanet Journal of Rare Diseases - February 22, 2021 Category: Internal Medicine Authors: Allison Mazzella, Mary Curry, Lisa Belter, Ros ángel Cruz and Jill Jarecki Tags: Research Source Type: research