Do we always need to treat patients with spinal muscular atrophy? A personal view and experience
We report the clinical outcomes observed in our patients with SMA type 1 or 2 receiving nusinersen, and we comment on the ethical implications of this treatment, in line with our results and those reported by ...
Source: Orphanet Journal of Rare Diseases - Category: Internal Medicine Authors: Caterina Agosto, Eleonora Salamon, Antuan Divisic, Francesca Benedetti, Luca Giacomelli, Aashni Shah, Giorgio Perilongo and Franca Benini Tags: Letter to the Editor Source Type: research