Gaucher Disease Type 1 patients from the ICGG Gaucher Registry sustain initial clinical improvements during twenty years of imiglucerase treatment

Publication date: Available online 8 January 2021Source: Molecular Genetics and MetabolismAuthor(s): Neal J. Weinreb, José Simon Camelo, Joel Charrow, Monica R. McClain, Pramod Mistry, Nadia Belmatoug, for the International Collaborative Gaucher Group (ICCG) Gaucher Registry (NCT00358943) investigators
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research