Gene Therapy Targeting the Inner Retina Rescues the Retinal Phenotype in a Mouse Model of CLN3 Batten Disease

Human Gene Therapy,Volume 31, Issue 13-14, Page 709-718, July 2020.

Source: Human Gene Therapy - July 14, 2020 Category: Genetics & Stem Cells Authors: Sophia-Martha kleine Holthaus Mikel Aristorena Ryea Maswood Olha Semenyuk Justin Hoke Aura Hare Alexander J. Smith Sara E. Mole Robin R. Ali Source Type: research