Dose Range Finding Studies with Two RPGR Transgenes in a Canine Model of X-Linked Retinitis Pigmentosa Treated with Subretinal Gene Therapy

Human Gene Therapy, Ahead of Print.

Source: Human Gene Therapy - June 28, 2020 Category: Genetics & Stem Cells Authors: Chunjuan Song Val érie L. Dufour Artur V. Cideciyan Guo-Jie Ye Malgorzata Swider Judith A. Newmark Adrian M. Timmers Paulette M. Robinson David R. Knop Jeffrey D. Chulay Samuel G. Jacobson Gustavo D. Aguirre William A. Beltran Mark S. Shearman Source Type: research