Neonatal combination therapy improves some of the clinical manifestations in the Mucopolysaccharidosis type I murine model

Publication date: Available online 11 May 2020Source: Molecular Genetics and MetabolismAuthor(s): Ludovica Santi, Giada De Ponti, Giorgia Dina, Alice Pievani, Alessandro Corsi, Mara Riminucci, Shaukat Khan, Kazuki Sawamoto, Laura Antolini, Silvia Gregori, Andrea Annoni, Andrea Biondi, Angelo Quattrini, Shunji Tomatsu, Marta Serafini
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research