Earlier and higher dosing of alglucosidase alfa improve outcomes in patients with infantile-onset Pompe disease: Evidence from real-world experiences

Publication date: June 2020Source: Molecular Genetics and Metabolism Reports, Volume 23Author(s): Yin-Hsiu Chien, Wen-Hui Tsai, Chaw-Liang Chang, Pao-Chin Chiu, Yen-Yin Chou, Fuu-Jen Tsai, Siew-Lee Wong, Ni-Chung Lee, Wuh-Liang Hwu

Source: Molecular Genetics and Metabolism Reports - April 30, 2020 Category: Genetics & Stem Cells Source Type: research