Hematopoietic stem cell transplantation in mucopolysaccharidosis type IIIA: A case description and comparison with a genotype-matched control group

Publication date: June 2020Source: Molecular Genetics and Metabolism Reports, Volume 23Author(s): Anja F. Köhn, Lorenz Grigull, Marcel du Moulin, Sarah Kabisch, Luise Ammer, Cornelia Rudolph, Nicole M. Muschol
Source: Molecular Genetics and Metabolism Reports - Category: Genetics & Stem Cells Source Type: research