OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)
Conditions: Lysosomal Storage Diseases; Metachromatic Leukodystrophy Intervention: Genetic: OTL-200 Sponsors: Orchard Therapeutics; Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials