OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)

Conditions:   Lysosomal Storage Diseases;   Metachromatic Leukodystrophy Intervention:   Genetic: OTL-200 Sponsors:   Orchard Therapeutics;   Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials