The deletion of mutant SOD1 via CRISPR/Cas9/sgRNA prolongs survival in an amyotrophic lateral sclerosis mouse model
Gene Therapy, Published online: 09 December 2019; doi:10.1038/s41434-019-0116-1The deletion of mutant SOD1 via CRISPR/Cas9/sgRNA prolongs survival in an amyotrophic lateral sclerosis mouse model
Source: Gene Therapy - Category: Genetics & Stem Cells Authors: Weisong Duan Moran Guo Le Yi Yakun Liu Zhongyao Li Yanqin Ma Guisen Zhang Yaling Liu Hui Bu Xueqin Song Chunyan Li Source Type: research