Rational Engineering and Preclinical Evaluation of Neddylation and SUMOylation Site Modified Adeno-Associated Virus Vectors in Murine Models of Hemophilia B and Leber Congenital Amaurosis

Human Gene Therapy, Ahead of Print.

Source: Human Gene Therapy - November 27, 2019 Category: Genetics & Stem Cells Authors: Shubham Maurya Bertin Mary Giridhara R. Jayandharan Source Type: research