A Phase 2 Study to Evaluate the Safety, Tolerability, PK and PD in Cystic Fibrosis Patients With at Least 1 G542X Allele

Conditions:   Genetic Disease;   Nonsense Mutation;   Cystic Fibrosis With Meconium Ileus Intervention:   Drug: ELX-02 Sponsor:   Eloxx Pharmaceuticals, Inc. Recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials