Safety and Proof-of-Concept (POC) Study With AMT-130 in Adults With Early Manifest Huntington Disease

Condition:   Huntington Disease Interventions:   Genetic: rAAV5-miHTT;   Procedure: Imitation surgery Sponsor:   UniQure Biopharma B.V. Not yet recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials