Sma treatments

Nusinersen has to be repeatedly administered intrathecally in patients with spinal muscular atrophy (SMA). The development of scoliosis is a complication associated with these patients and may limit the administration of treatment. Describe our experience in the administration of intrathecal medication in patients with SMA. We propose a strategy that allows the intrathecal approach in patients with severe scoliosis. Prospective observational study. We collected demographic data related to the disease and the intrathecal administration procedure in patients with SMA treated with nusinersen from March 2018 to March 2019.
Source: Neuromuscular Disorders - Category: Neurology Authors: Source Type: research