In Vivo Gene Therapy for Mucopolysaccharidosis Type III (Sanfilippo Syndrome): A New Treatment Horizon

Human Gene Therapy,Volume 30, Issue 10, Page 1211-1221, October 2019.

Source: Human Gene Therapy - September 23, 2019 Category: Genetics & Stem Cells Authors: Sara Marc ó Virginia Haurigot Fatima Bosch Source Type: research