Dual ABCA4-AAV Vector Treatment Reduces Pathogenic Retinal A2E Accumulation in a Mouse Model of Autosomal Recessive Stargardt Disease

Human Gene Therapy, Ahead of Print.

Source: Human Gene Therapy - September 29, 2019 Category: Genetics & Stem Cells Authors: Frank M. Dyka Laurie L. Molday Vince A. Chiodo Robert S. Molday William W. Hauswirth Source Type: research