Intrathecal administration of nusinersen in adult and adolescent patients with spinal muscular atrophy and scoliosis: transforaminal versus conventional approach.

Spinal Muscular Atrophy (SMA) is one of the most common neuromuscular disorders in childhood with an incidence of 1:10,000 [1] and the first genetic cause of infant mortality.

Source: Neuromuscular Disorders - August 22, 2019 Category: Neurology Authors: Sara Bortolani, Guido Stura, Giancarlo Ventilii, Liliana Vercelli, Enrica Rolle, Federica Ricci, Mauro Bergui, Tiziana Mongini Source Type: research