Long-term efficacy and safety of sirolimus therapy in patients with lymphangioleiomyomatosis

Sirolimus has been confirmed to be effective for lymphangioleiomyomatosis (LAM), a rare multisystem neoplastic disease in women. The long-term effects of sirolimus treatment for LAM, however, are largely unkno...

Source: Orphanet Journal of Rare Diseases - August 20, 2019 Category: Internal Medicine Authors: Siqi Hu, Xiuxiu Wu, Wenshuai Xu, Xinlun Tian, Yanli Yang, Shao-Ting Wang, Song Liu, Xingxiang Xu and Kai-Feng Xu Tags: Research Source Type: research