Efficacy and Safety of Dichlorphenamide for Primary Periodic Paralysis in Adolescents Compared With Adults

Primary periodic paralyses (PPP) are a group of rare, hereditary skeletal muscle diseases characterized by episodic muscle weakness. Dichlorphenamide (DCP) for PPP was effective and well tolerated in two randomized, double-blind, placebo-controlled studies, including one with adolescents. This analysis describes effects of DCP among adolescents and adults.

Source: Pediatric Neurology - August 6, 2019 Category: Neurology Authors: Emma Ciafaloni, Fredric Cohen, Robert Griggs Tags: Research Paper Source Type: research