Hereditary transthyretin amyloidosis: a model of medical progress for a fatal disease

Nature Reviews Neurology, Published online: 17 June 2019; doi:10.1038/s41582-019-0210-4In this Review, Adams et al. discuss the latest insights into various aspects of hereditary transthyretin amyloidosis and its management, including its epidemiology, pathogenesis and the latest success with RNA interference and antisense oligonucleotide therapies.
Source: Nature Reviews Neurology - Category: Neurology Authors: Source Type: research