The Alpha-1-Antitrypsin Promoter Improves the Efficacy of an AAV Vector for the Treatment of MNGIE

Human Gene Therapy, Ahead of Print.

Source: Human Gene Therapy - April 23, 2019 Category: Genetics & Stem Cells Authors: Raquel Cabrera-P érez Ferran Vila-Juli à Michio Hirano Federico Mingozzi Javier Torres-Torronteras Ramon Mart í Source Type: research