Emerging Therapeutic Approaches for Diamond Blackfan Anemia.

We present different DNA- and RNA-based technologies as well as new candidate pharmacological treatments and discuss their relevance and potential applicability for the cure of DBA.
PMID: 30411682 [PubMed - as supplied by publisher]

Source: Current Gene Therapy - November 9, 2018 Category: Genetics & Stem Cells Authors: Aspesi A, Borsotti C, Follenzi A Tags: Curr Gene Ther Source Type: research