New nusinersen drug delivery method identified for spinal muscular atrophy patients

(Clinic for Special Children) A new report has identified an alternative method to deliver nusinersen to patients with spinal muscular atrophy (SMA) using a subcutaneous intrathecal catheter system (SIC) configured by connecting an intrathecal catheter to an implantable infusion port. SMA is a devastating genetic disease that leads to progressive degeneration of motor neurons that control movement, swallowing, and breathing. It is the leading genetic cause of infant death worldwide.
Source: EurekAlert! - Medicine and Health - Category: International Medicine & Public Health Source Type: news