New results support continued development of AAV-based human factor VIII gene therapy

(Mary Ann Liebert, Inc./Genetic Engineering News) Gene therapy using an optimized adeno-associated virus (AAV) to deliver the human fac-tor VIII gene to cynomolgus macaques showed a substantial increase in hFVIII expres-sion and no detectable antibody response for 30 weeks in some animals.
Source: EurekAlert! - Biology - Category: Biology Source Type: news