Oligonucleotides Hold Promise as a Therapy for Friedreich's Ataxia: Friedreich's ataxia currently is incurable, but synthetic antisense oligonucleotides have demonstrated promising results in increasing frataxin gene expression and restoring it to normal levels

American Journal of Medical Genetics Part A,Volume 176, Issue 6, Page 1282-1282, June 2018.
Source: American Journal of Medical Genetics Part A - Category: Genetics & Stem Cells Source Type: research