Amelioration of Alpha-1 Antitrypsin Deficiency Diseases with Genome Editing in Transgenic Mice

Human Gene Therapy, Ahead of Print.

Source: Human Gene Therapy - June 22, 2018 Category: Genetics & Stem Cells Authors: Shen Shen Minerva E. Sanchez Keith Blomenkamp Erik M. Corcoran Eugenio Marco Clifford J. Yudkoff Haiyan Jiang Jeffrey H. Teckman David Bumcrot Charles F. Albright Source Type: research