A Gene Therapy Appears ToReplaceMissing ProteinIn Muscular Dystrophy Patients

An experimental gene therapy appeared to dramatically increase the production of a muscle-making protein in three young boys with Duchenne muscular dystrophy, a deadly and irreversible disease, according to results being presented by the drugmaker Sarepta Therapeutics at an investor event.

Source: Forbes.com Healthcare News - June 19, 2018 Category: Pharmaceuticals Authors: Matthew Herper, Forbes Staff Tags: NASDAQ:SLDB NASDAQ:SRPT NYSE:PFE Source Type: news