In child-crippling mucolipidosis IV, drug shows hope in lab cultures

(Georgia Institute of Technology) Medicine offers no treatment for children crippled by mucolipidosis IV, which hits them in the first year of life and gradually becomes fatal. But researchers battling it with limited means at their disposal have captured a glimmer of hope in lab tests on an existing drug.
Source: EurekAlert! - Medicine and Health - Category: International Medicine & Public Health Source Type: news