Gene therapy for lipoprotein lipase deficiency yields promising results

(Mary Ann Liebert, Inc./Genetic Engineering News) During the first 18 months after treatment with alipogene tiparvovec, a gene therapy recently approved in Europe to treat lipoprotein lipase deficiency (LPLD), the first patient to receive the treatment had no abdominal pain or episodes of pancreatitis, following a history of 37 pancreatitis attacks.
Source: EurekAlert! - Biology - Category: Biology Source Type: news