Pre-Symptomatic Study of Intravenous AVXS-101 in Spinal Muscular Atrophy (SMA) for Patients With Multiple Copies of SMN2

Condition:   Spinal Muscular Atrophy Intervention:   Biological: AVXS-101 Sponsor:   AveXis, Inc. Recruiting

Source: ClinicalTrials.gov - April 23, 2018 Category: Research Source Type: clinical trials