First gene therapy treatment to stave off childhood degenerative brain disease wins national clinical excellence award

(Burness) The Clinical Research (CR) Forum, a non-profit membership association of top clinical research experts and thought leaders from the nation's leading academic health centers, today awarded its most prestigious honor to a Massachusetts General Hospital research team for its discovery of the first successful gene therapy treatment for a fatal brain disease, cerebral adrenoleukodystrophy (ALD).
Source: EurekAlert! - Medicine and Health - Category: International Medicine & Public Health Source Type: news