Targeted in vivo knock-in of human alpha-1-antitrypsin cDNA using adenoviral delivery of CRISPR/Cas9
Targeted in vivo knock-in of human alpha-1-antitrypsin cDNA using adenoviral delivery of CRISPR/Cas9Targeted in vivo knock-in of human alpha-1-antitrypsin cDNA using adenoviral delivery of CRISPR/Cas9, Published online: 27 March 2018; doi:10.1038/s41434-018-0003-1Targeted in vivo knock-in of human alpha-1-antitrypsin cDNA using adenoviral delivery of CRISPR/Cas9
Source: Gene Therapy - Category: Genetics & Stem Cells Authors: Calvin J. Stephens Elena Kashentseva William Everett Lyudmila Kaliberova David T. Curiel Source Type: research