New drug improves motor function of children with genetic disorder

(Nemours) Children with later-onset spinal muscular atrophy (SMA) were more likely to show gains in motor function when treated with a new medication compared to children receiving a sham procedure, according to a study published today in the New England Journal of Medicine. The study demonstrates the impact the drug, nusinersen, can have on older patients with this progressive neuromuscular disorder.
Source: EurekAlert! - Medicine and Health - Category: International Medicine & Public Health Source Type: news