FDA Considers Gene Therapy for Rare Eye Disease

If approved, it would be only the 2nd gene therapy OK'd in the United States
Source: WebMD Health - Category: Consumer Health News Source Type: news

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Authors: Yan X, Zhou Z, Guo L, Zeng Z, Guo Z, Shao Q, Xu W Abstract Bone fractures are a worldwide public health concern. Previous studies have demonstrated that bone morphogenetic protein-7 (BMP7) gene transfer or mesenchymal stem cells (MSCs) transplantation may be a promising novel therapeutic approach. Therefore, the aim of the present study was to observe the effect of bone BMP7 transfer to MSCs on fracture healing. Bone marrow-derived MSCs (BMSCs) from New Zealand white rabbits were isolated and identified using flow cytometry. A recombinant BMP7 overexpressing adenovirus vector (Adv) was constructed and tran...
Source: Experimental and Therapeutic Medicine - Category: General Medicine Tags: Exp Ther Med Source Type: research
NIH oversight panel no longer plans to review all applications for gene therapy experiments
Source: The Doctors Lounge - Psychiatry - Category: Psychiatry Tags: Cardiology, Dermatology, Endocrinology, Family Medicine, Geriatrics, Gastroenterology, Gynecology, Infections, AIDS, Internal Medicine, Allergy, Nephrology, Neurology, Oncology, Ophthalmology, Orthopedics, ENT, Pathology, Pediatrics, Pharmacy, Psychiatry, Source Type: news
Source: Chemical and Engineering News - Category: Chemistry Authors: Source Type: research
Source: Chemical and Engineering News - Category: Chemistry Authors: Source Type: research
FRIDAY, Aug. 17, 2018 -- A U.S. National Institutes of Health oversight panel will no longer review all applications for gene therapy experiments. Instead, the panel will assume an advisory role, while the U.S. Food and Drug Administration will...
Source: Drugs.com - Pharma News - Category: Pharmaceuticals Source Type: news
Use of Precision-Cut Lung Slices as an Ex Vivo Tool for Evaluating Viruses and Viral Vectors for Gene and Oncolytic Therapy. Mol Ther Methods Clin Dev. 2018 Sep 21;10:245-256 Authors: Rosales Gerpe MC, van Vloten JP, Santry LA, de Jong J, Mould RC, Pelin A, Bell JC, Bridle BW, Wootton SK Abstract Organotypic slice cultures recapitulate many features of an intact organ, including cellular architecture, microenvironment, and polarity, making them an ideal tool for the ex vivo study of viruses and viral vectors. Here, we describe a procedure for generating precision-cut ovine and murine tissue ...
Source: Clinical Lung Cancer - Category: Cancer & Oncology Authors: Tags: Mol Ther Methods Clin Dev Source Type: research
Conditions:   Relapsed Neuroblastoma;   Refractory Neuroblastoma Interventions:   Genetic: C7R-GD2.CART cells;   Drug: Cyclophosphamide;   Drug: Fludarabine Sponsors:   Baylor College of Medicine;   Texas Children's Hospital;   Center for Cell and Gene Therapy, Baylor College of Medicine Not yet recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials
Reuters Health Information
Source: Medscape Medical News Headlines - Category: Consumer Health News Tags: Medscape Today News Source Type: news
Will Woleben, six, from McKinney, Texas, was diagnosed with Leigh syndrome in April 2014. Now his parents are working to raise $300,000 to enroll him in a gene therapy trial.
Source: the Mail online | Health - Category: Consumer Health News Source Type: news
THURSDAY, Aug. 16, 2018 -- A U.S. National Institutes of Health oversight panel will no longer review all applications for gene therapy experiments, according to a perspective piece published online Aug. 15 in the New England Journal of...
Source: Drugs.com - Pharma News - Category: Pharmaceuticals Source Type: news
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