Mini form of replacement gene can delay degeneration in leber congenital amaurosis

(Mary Ann Liebert, Inc./Genetic Engineering News) A new study demonstrates success in using a shortened form of the CEP290 gene for gene therapy in a mouse model of Leber congenital amaurosis type 10 (LCA10), a retinal degenerative disorder that causes childhood blindness.
Source: EurekAlert! - Medicine and Health - Category: International Medicine & Public Health Source Type: news