MDA and CMTA fund grant to study gene therapy in charcot-marie-tooth disease

(Charcot-Marie-Tooth Association) The Muscular Dystrophy Association (MDA) and the Charcot-Marie-Tooth Association (CMTA) March 17 announced a research grant totaling $119,999 to Kleopas Kleopa, M.D., for a study on the effectiveness of a gene therapy approach in CMT1X. In an earlier study, Kleopa and his colleagues showed that a single injection of the gene that is mutated in CMT1X was associated with production of normal protein in nerves and improvement of peripheral nerve health and motor performance.
Source: EurekAlert! - Medicine and Health - Category: Global & Universal Source Type: news