Novel treatments for rare rheumatologic disorders: analysis of the impact of 30 years of the US orphan drug act
Rare rheumatologic diseases are a heterogeneous group of conditions associated with high morbidity. As a whole group, rare rheumatologic diseases afflict millions of people demanding for effective therapies. T...
Source: Orphanet Journal of Rare Diseases - Category: Internal Medicine Authors: Evangelos Minos, Robert J. Barry, Sue Southworth, Annie Folkard, Philip I. Murray, Jay S. Duker, Pearse A. Keane, Alastair K. Denniston, Thomas Lutz, Anette Lampert, Georg F. Hoffmann and Markus Ries Source Type: research