Disease burden of spinal muscular atrophy in Germany
This study aimed at analyzing the economic burden and disease-specific health-related quality of life (HRQOL) of patients with spinal muscular atrophy (SMA) in Germany. SMA is a so far non-curable neuromuscula...
Source: Orphanet Journal of Rare Diseases - Category: Internal Medicine Authors: Constanze Klug, Olivia Schreiber-Katz, Simone Thiele, Elisabeth Schorling, Janet Zowe, Peter Reilich, Maggie C. Walter and Klaus H. Nagels Source Type: research