Gene therapy for cystic fibrosis shows encouraging trial results

A therapy that replaces the faulty gene responsible for cystic fibrosis in patients’ lungs has produced encouraging results in a major UK trial. Cystic fibrosis (CF) is the commonest lethal inherited disease in the UK, affecting around 10,000 people nationally and over 90,000 worldwide. Patients’ lungs become filled with thick, sticky mucus making them vulnerable...
Source: NIHR Evaluation, Trials and Studies News - Category: American Health Source Type: news