CRISPR Gene Editing Takes Next Step in TTR Amyloidosis CRISPR Gene Editing Takes Next Step in TTR Amyloidosis

A phase 1 study showed robust responses in patients with TTR amyloidosis with cardiomyopathy, similar to those reported last year in amyloid polyneuropathy.Medscape Medical News
Source: Medscape Cardiology Headlines - Category: Cardiology Tags: Cardiology News Source Type: news